The most commonly diagnosed form of muscular dystrophy, Duchenne is a genetic disease that affects mostly boys and causes progressive muscle weakness over time. Its early physical signs tend to be ...

An experimental RNA therapy from Avidity Biosciences has early clinical trial results showing it reduced by half the expression of a gene at the root of a rare, inherited form of muscular dystrophy ...

Muscular dystrophy is a group of inherited conditions that lead to progressive weakening of voluntary muscles and, in some cases, impact the heart and other organs. There are nine major types of ...

Myotonic muscular dystrophy, which is sometimes called myotonic dystrophy, is a type of muscular dystrophy. There are two types of myotonic muscular dystrophy, described as type 1 (DM 1) and type 2 ...

Congenital muscular dystrophy (CMD) is a disease that affects certain muscles. Individuals with CMD may experience symptoms such as muscle weakness and joint problems. “Congenital” means present since ...

Oculopharyngeal muscular dystrophy (OPMD) is a rare inherited disorder that causes weakness in the eye and throat muscles. It may lead to drooping eyelids and swallowing difficulties. Muscular ...

At Binghamton University, researchers were among the first to find ways to help patients with Duchenne muscular dystrophy (DMD) through the development of an effective drug. Now, they are continuing ...