Risto-cel, a gene-edited cell therapy formerly called BEAM-101, for severe SCD, benefits patients for nearly two years, new ...
A lack of accessibility in a non-inclusive society for those with a disability comes at a terrible cost, writes columnist.
Casgevy safely and effectively prevents vaso-occlusive crises in children ages 5 to 11 with severe sickle cell disease, trial ...
VAS‑101, a skin gel containing curcumin, was shown to partially reverse impairments to the powerhouses of cells in the hearts ...
Low socioeconomic status is not significantly associated with a higher risk for stroke in children with sickle cell disease, ...
Sickle cell disease (SCD) may be cured in some individuals by a stem cell transplant. There also are several approved therapies to help manage the condition and its related complications. Some of the ...
A study of children with sickle cell disease (SCD) referred for an evaluation of neuropsychological deficits found that while 19 of 89 patients (25%) were diagnosed with attention deficit ...
A new, interactive application touted as the first of its kind can help people with sickle cell disease (SCD) learn about and communicate with their care team about their pain attacks. People with ...
The European Medicines Agency (EMA) has confirmed the continuing suspension of marketing authorization for Pfizer’s sickle cell disease (SCD) treatment Oxbryta (voxelotor) — withdrawn from the market ...
Naproxcinod, an investigational therapy being developed by Fera Pharmaceuticals as a treatment for sickle cell disease (SCD), has been granted orphan drug designation by the U.S. Food and Drug ...
Using tocilizumab off-label in four young adults with sickle cell disease (SCD) who developed hyperhemolysis syndrome as a complication of a blood transfusion stopped the premature destruction of red ...