Risto-cel, a gene-edited cell therapy formerly called BEAM-101, for severe SCD, benefits patients for nearly two years, new ...
A lack of accessibility in a non-inclusive society for those with a disability comes at a terrible cost, writes columnist.
Casgevy safely and effectively prevents vaso-occlusive crises in children ages 5 to 11 with severe sickle cell disease, trial ...
VAS‑101, a skin gel containing curcumin, was shown to partially reverse impairments to the powerhouses of cells in the hearts ...
Low socioeconomic status is not significantly associated with a higher risk for stroke in children with sickle cell disease, ...
As part of a program to support children with sickle cell disease (SCD) and cancers, supplemental insurance company Aflac has released a new children’s book that aims to illustrate how empathy and ...
Researchers have identified a new method to reactivate fetal hemoglobin, without the need for gene-editing therapy, that has the potential to treat more people with sickle cell disease (SCD) at a ...
Disc Medicine has launched a small clinical trial to test DISC-3405, its treatment candidate for reducing iron levels and easing iron overload, in people with sickle cell disease (SCD). The Phase 1b ...
Sickle cell disease presents a range of complications, some of which are visible while others are invisible. For the first two decades of my life, I only dealt with invisible complications, which ...
A new oral treatment, mitapivat, for sickle cell disease (SCD) significantly boosted hemoglobin levels in patients over a year, achieving one of the primary goals of a Phase 3 clinical trial. In the ...
Today, I woke up with a severe headache — again! It’s been four long, exhausting weeks of feeling like someone has set up camp behind my eyes with a hammer. The ache pulses before I’m even fully ...