Columnist Ari Anderson pays tribute to his mom, who excels at many roles, including advocate, manager, teacher, and caregiver ...

Sixteen years after her daughter's diagnosis of SMA type 1, guest columnist Cherie Ehlert is no longer counting the months, ...

Cherie Ehlert lives in Vancouver, British Columbia, Canada. She is a disability advocate and created “Charlie's Angels” to ...

SMA gene therapy Zolgensma safely improved motor function in children with SMA who needed tracheostomy, a real-world study ...

Columnist Helen Baldwin finds the perfect gift for her granddaughter's birthday, one of the many unexpected blessings in her ...

Columnist Connie Chandler writes about her family's tradition of baking and decorating holiday cookies, a project that SMA ...

Fatigue in the diaphragm may contribute to breathing issues in people with spinal muscular atrophy, a new study reports.

Columnist Connie Chandler gives thanks for the acts of kindness her caregivers perform — the sweet stuff that makes life so ...

The specialty pharmacy Orsini was selected as a partner to provide Itvisma, the newly approved gene therapy for people with ...

FDA approved Itvisma, a one-time gene therapy for SMA patients ages 2 and older. Itvisma restores SMN protein, improving motor function and reducing treatment burden. A Novartis executive says the ...

Columnist Sherry Toh prefers holiday giving rather than receiving and making others happy, because what she wants isn't found in stores.